gene therapy

Muscular dystrophy-reversing gene therapy: Human trials in 2 years

Posted in Medicine, Science on 23rd Jul, 2024
by Alex Muller

A new gene therapy for Duchenne muscular dystrophy shows promise in halting and potentially reversing muscle damage.

An AI Tool Just Revealed Almost 200 New Systems For CRISPR Gene Editing

Posted in Medicine, Science on 29th Nov, 2023
by Alex Muller

This month, a team at MIT and Harvard led by CRISPR pioneer Dr. Feng Zhang took inspiration from an existing big-data approach and used AI to narrow the sea of genetic sequences to a handful that are similar to known CRISPR systems.

New research advances understanding of cancer risk in gene therapies

Posted in Medicine on 20th Nov, 2023
by Alex Muller

The gene therapy treatment itself is not the likely cause of new DNA mutations in blood stem cells.

CRISPR enters its first human clinical trials

Posted in Medicine, Science on 18th Aug, 2019
by Alex Muller

In the first spate of clinical trials, scientists are using CRISPR/Cas9 to combat cancer and blood disorders in people.

Breakthrough crispr gene editing trial set to begin this year

Posted in Science on 17th Apr, 2018
by Alex Muller

Biotech company CRISPR Therapeutics is set to treat Europes patients with the CRISPR gene-editing tool this year following regulatory approval for trials.